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  1. ProQR update and additional sepofarsen Illuminate trial analyses

    News update

    … review designed to deliver on our commitment to advance RNA therapies for diseases with high unmet need. We are also … Agency (EMA) and US Food & Drug Administration (FDA). RNA editing technology – accelerate development of the …

    ProQR logo on the left. The word update on the right.

  2. ProQR Analyst Event

    Webcast

    During this webcast ProQR leadership will highlight key advancements from its clinical-stage pipeline and Axiomer® RNA editing platform.

  5. Always excited about RNA therapies

    Story

    … Always excited about RNA therapies He is one of the founders of ProQR, but even … to choose RNA therapy over gene therapy or even gene editing using CRISPR-Cas, the latest hype. And the main … are still expanding our toolbox. We can now do single base RNA editing, turning a single A nucleotide into an I. It …

    A photo of Gerard Platenburg

  8. ProQR Announces Presentations at the OTS Annual Meeting

    Press release

    … to changing lives through the creation of transformative RNA medicines for the treatment of severe genetic rare … 10 (LCA10). Presentation title :  Proof-of-concept for RNA-editing oligonucleotide QR-110 for treatment of inherited …

  9. ProQR Announces Financial Results for the Third Quarter of 2018

    Press release

    … to changing lives through the creation of transformative RNA medicines for the treatment of severe genetic rare … with LCA10 and preclinical data for ProQR’s Axiomer ® RNA-editing technology. Abstract titles: ○   Proof-of-concept …