This presentation reviews Axiomer editing oligonucleotides (EONs) structure activity, the potential of Axiomer platform as well as its applicability for the treatment of liver originated disorders.
The Eye on the Future Forum (EFF) is a platform hosted by ProQR on innovative clinical development approaches for genetic eye diseases. This Fall Summit will explore the Science of RNA Therapies.
The presentation reviews EONs structure activity, the potential of the Axiomer platform as well as its applicability for the treatment of liver originated disorders. Presented at TIDES USA on May 9, 2023 by Gerard Platenburg - ProQR Therapeutics.
… type 10 (LCA10) ARVO 2021 presentation by Stephen R. Russell from Iowa University on the Safety and efficacy of … Leber Congenital Amaurosis type 10. Author(s) Stephen R. Russell 1 , Arlene V. Drack 1 , Artur V. Cideciyan 2 , … The Children’s Hospital of Philadelphia, PA, USA; 5 ProQR Therapeutics, Leiden, the Netherlands …
