… ProQR Announces Publication in Nature Medicine for Sepofarsen in Leber Congenital Amaurosis 10 LEIDEN, … after a single treatment with antisense oligonucleotide sepofarsen: a case report ” describing durable vision …
… Top-Line Results from Phase 2/3 Illuminate Trial of Sepofarsen in CEP290-mediated LCA10 Study did not meet … 12. “Given the results observed in earlier studies of sepofarsen, the Illuminate trial results are unexpected and …
Agreement provides ProQR with initial payment of €12.5M and up to €135M in further payments, as well as potential additional earn outs based on commercial sales in the US and EU
Divestment of sepofarsen and ultevursen supports ProQR’s strategic focus on the Axiomer®&
… ProQR Completes Enrollment of its Pivotal Trial of Sepofarsen for the Treatment of LCA10 Top-line results expected H1 2022 Sepofarsen is a potential first-in-class RNA therapy for the …
… ProQR Announces Virtual Presentation of Phase 1/2 Sepofarsen Extension Trial Data at the Association for … from the Company’s Phase 1/2 InSight extension trial of sepofarsen and live Q&A session at the Association for …
Call on July 20 will include a snapshot from the ongoing InSight open-label extension study of sepofarsen, including preliminary second eye treatment data
… Completed 12 Month Visit in Phase 2/3 Illuminate Trial of Sepofarsen Top-line data now expected to be announced in Q1 2022 Sepofarsen is a potential first-in-class RNA therapy for the …
Reported rapid, significant and durable improvements in vision at twelve months
Concordant improvement in key secondary outcome measures
The target registration dose of sepofarsen was well-tolerated with a favorable benefit/risk profile
Strengthens confidence
Post-hoc analyses from Illuminate trial of sepofarsen demonstrate an encouraging efficacy signal when comparing active treatment and sham eyes to their corresponding contralateral eyes across multiple endpoints – Company plans to discuss findings with regulators in Q3
… ProQR Announces Virtual Presentation of Phase 1/2 Sepofarsen Data Through the Association for Research in … presentation of data from the Company’s Phase 1/2 trial of sepofarsen. The data will be shared via a video presentation …