Presented at the Deaminet 2024 Conference on January 18, 2024 by Gerard Platenburg - ProQR Therapeutics
Axiomer™ an RNA editing technology, Building confidence towards clinical development, Deaminet 2024
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The 5th International Conference on Base Editing, Prime Editing & Related Enzymes (Deaminet 2024) in San Diego, California featured an update by ProQR on the Axiomer™ platform. This presentation features new in vivo data for ProQR's proprietary Axiomer™ RNA editing technology platform demonstrating robust editing of ACTB in the liver of NHP, as well as functional protein data with the liver target ANGPTL3 in mice. These new preclinical platform data further highlight the potential of Axiomer™ EONs in preparation for clinical development and supporting discovery of potential new therapeutic applications.