Oral presentation title: Therapeutic potential of an RNA editing platform using Editing Oligonucleotides (EONs)
Presenter: Gerard Platenburg, CSO and co-founder, ProQR Therapeutics
Session: Oligonucleotide Discovery and Delivery - Optimizing Design, Delivery and Performance
Date: Tuesday, March 14 – 9:35 am EDT
Abstract: Axiomer, an RNA editing technology, uses Editing Oligonucleotides (EONs) to target specific RNA for A-to-I editing by recruiting endogenous Adenosine Deaminase Acting on RNA (ADAR). This presentation will highlight the therapeutic possibilities of this platform that are not limited to disease causing mutations and can potentially address high unmet medical needs by editing wild-type RNA to engineer proteins or modify their function as well as creating de novo mutations.
Panel session title: Integrating Innovative Technologies into Oligo Therapeutics Discovery and Delivery
Presenter: Gerard Platenburg, CSO and co-founder, ProQR Therapeutics
Session: Oligonucleotide Discovery and Delivery - Optimizing Design, Delivery and Performance
Date: Tuesday, March 14 – 10:05 am EDT